Miracle Pill Brings Hope to Cystic Fibrosis Patients
Children's Hospital Colorado patient, Dylan Fontana, 6, was born with cystic fibrosis, a disease that causes the body to build up mucus in the lungs, which causes breathing and digestion problems. Up until recently, there was no sign of a cure.
On Jan. 31, The Food and Drug Administration (FDA) approved a pill named Kalydeco, the first drug that treats the underlying causes of cystic fibrosis. "A lot of this is not understood, but we know [the drug] works," Frank Accurso, director of the Cystic Fibrosis Center at Children's Colorado said, "and we do believe that starting younger is better."
Although the pill has been approved by the FDA, it is not a cure for everyone, and Dylan is lucky that he has the right genetic mutation to take the pill. Subsequently, the Fontana family is thankful. In the future, and if research is successful, Dr. Accurso hopes that the pill will serve as a springboard to serving other CF patients--even those with a different CF mutation.
Read more about how the new drug is improving Dylan's condition.
Learn more about cystic fibrosis treatment at Children's Colorado.