Research and Innovation in Pediatric Medicine (S3:E54)

On several Charting Pediatrics podcasts, we have discussed various topics related to the clinical application of research discoveries, such as the advent of CAR-T cell therapy for pediatric leukemia and the new class of targeted therapies that are going to transform our care of children with cystic fibrosis.

Listen to a pediatric expert discuss pediatric research breakthroughs

In this episode, we are privileged to have John Barnard, MD, join us to discuss exciting pediatric research breakthroughs in the fields of genomics, gene therapy and more. Dr. Barnard joins us from Nationwide Children’s Hospital where he serves as the Chief of Pediatrics, President of The Research Institute and holds the Ann I. Wolfe Endowed Chair in Pediatric Research Leadership. He is also the chair of the Department of Pediatrics and professor of Pediatrics, Gastroenterology, Hepatology and Nutrition at The Ohio State University College of Medicine.

In this episode, our experts discuss:

• Some of the most important advances that have positively impacted kids, such as genomics and gene therapy
• The singular advance that’s taken gene therapeutics from the 90s to where we are today
• A new gene therapy called Zolgensma for spinal muscular atrophy discovered at Nationwide Children’s Hospital
• How we can make these effective, yet expensive gene therapeutics available to kids who need them
• Important decisions on the federal level regarding coverage for gene therapeutics as more of them come onto the market
• National research priorities in pediatric health
• The intersection of mental health research and what is driving increased mental health needs in pediatric practices

Pediatric research at Children’s Hospital Colorado

At Children’s Colorado, we're not just conducting transformative research for the sake of innovation. We're using research to pioneer treatments with the hope of eradicating childhood disease and changing pediatric medicine to give all kids a healthier future. Learn more about our pioneering pediatric research.